The analysts forecast global krabbe diseas`e treatment market to grow at a CAGR of 7.24% during the period 2018-2022. One trend in the market is emergence of pharmacological chaperone therapy.
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More than two-fifth known cases of Krabbe disease are due to missense mutation in the GLC enzyme.
Such mutations result in the disruption of enzyme folding and ultimately stops the GLC from reaching its site of action in enough amounts in the lysosome.
Major key players in the global krabbe disease treatment market: GlaxoSmithKline, Johnson & Johnson, and Novartis.
According to the krabbe disease treatment market report, one driver in the market is special drug designation. An important factor that is expected to drive market growth is the assignment of special drug designations to drugs and biologics that are intended for the safe and effective treatment of Krabbe disease.
The priority review program for facilitating fast drug approvals is offered by the Food and Drug Administration (FDA).
Further, the krabbe disease treatment market report states that one challenge in the market is limited patient pool for clinical trials. The prevalence rate of orphan diseases such as Krabbe is very low.
Therefore, the percentage of population affected by such diseases is also low in comparison with other disorders. This, in turn, restricts the number of patients available for clinical trial evaluation of drugs under development for the treatment of orphan diseases.
Key questions answered in this report:
What will the market size be in 2022 and what will the growth rate be?
What are the key market trends?
What is driving this market?
What are the challenges to market growth?
Who are the key vendors in this market space?
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Few Points from List of Exhibits:
Exhibit 1: Types of Krabbe disease
Exhibit 2: Parent market
Exhibit 3: Global rare diseases treatment market: Segmentation
Exhibit 4: Market characteristics
Exhibit 5: Market segments
Exhibit 6: Market definition: Inclusions and exclusions checklist
Exhibit 7: Market size
Exhibit 8: Validation techniques employed for market sizing 2017
Exhibit 9: Global Krabbe disease treatment market 2017-2022 ($ millions)
Exhibit 10: Global Krabbe disease treatment market: Year over year growth 2018-2022 (%)
Exhibit 11: Five forces analysis 2017
Exhibit 12: Five forces analysis 2022
Exhibit 13: Bargaining power of buyers
Exhibit 14: Bargaining power of suppliers
Exhibit 15: Threat of new entrants
Exhibit 16: Threat of substitutes
Exhibit 17: Threat of rivalry
Exhibit 18: Pipeline landscape by development phase
Exhibit 19: Key clinical trials for global Krabbe disease treatment market
Exhibit 20: Global Krabbe disease treatment market by therapy 2017-2022 (% share)